Small molecules: what are they, and why are they important? Small molecules are a type of therapeutic approach that our scientists explore in their research. Their small size allows them to enter cells to modulate certain biological processes. In this animation, learn more about how small molecules work and their potential to have a big impact on serious diseases.

Our goal at Vertex Pharmaceuticals is to discover innovative solutions to the most difficult scientific and medical problems. And that requires identifying the tools and technologies we think have the potential to transform serious diseases. Small molecules represent one approach that continues to fuel our research and development.

About this video series

This series shares the science behind some of the tools and technologies we use in our research and clinical development. As our scientists continue to make progress, we want to spread awareness about the innovative technology used behind the scenes in our labs. Check out some of the other tools in our toolbox that we are using to advance toward our goals: