Beta thalassemia

An image of Gaia, a patient living with beta thalassemia, smiling while walking across a city street


Every day, people living with serious diseases strive to be more than their disease — to be defined by what they can dream and hope and achieve, not by what limits them. Our commitment to people with serious diseases is uncompromising and goes beyond our research and development (R&D) and medicines. 

Working with the beta thalassemia community

We work with organizations that help people with transfusion-dependent beta thalassemia (TDT) live active, full lives.

We are committed to investigating and advancing approaches to treat the underlying cause of TDT. Vertex seeks to identify opportunities where we can support, empower, learn from and engage with the beta thalassemia community and ensure their voices are represented and incorporated into all that we do. 

An image of five Vertexians smiling at the camera while attending the Cooley's Anemia Walk

Vertexians with the thalassemia community in D.C. at the 2023 Cooley's Anemia Foundation Care Walk.

Supporting the beta thalassemia community

We are honored to support our beta thalassemia community partners to raise awareness and understanding of thalassemia, including Cooley’s Anemia Foundation, the Thalassemia International Federation and others. 



Learn about our work in beta thalassemia

To learn more about our beta thalassemia studies in the U.S., visit the clinical trials website. For information about non-U.S. sites, visit