Sickle cell disease

Every day, people living with serious diseases strive to be more than their disease — to be defined by what they can dream and hope and achieve, not by what limits them. Our commitment to people with serious diseases is uncompromising and goes beyond our research and development (R&D) and medicines.
Understanding sickle cell disease: Real stories, real impact
Meet sisters Nedda and Renna, the Dahn family and Kevin — all battling against sickle cell disease (SCD), a serious and life-shortening blood disorder. Watch the videos below to hear what it’s like to live with SCD, including the challenges and impacts of the disease.

Understanding SCD
Sisters, Nedda and Renna, from Sweden are both living with SCD. Find out more about their experiences and complications living with SCD.

Caring for three Sickle Cell Warriors
Mapillar Dahn is the mother of three daughters living with SCD. This video is a glimpse into the strength it takes to hold a family together with SCD.

Daily life with SCD
Kevin opens a window into what life truly looks like living with SCD. From small routines to big challenges, his story brings the reality of SCD to life.
Working with the SCD community
We are committed to investigating and advancing new approaches to treat SCD. To achieve that mission, we work with organizations that help people with SCD live active, full lives.
Vertex seeks to identify opportunities where we can support, empower and learn from the sickle cell community to ensure their voices are heard and represented in our work.

Dr. Lakiea Bailey, Sickle Cell Warrior, advocate, educator and CEO of the Sickle Cell Consortium, on a panel with Vertexian Dr. Bill Hobbs, VP, Clinical Development.
Supporting the SCD community
We are honored to support several sickle cell community partners to raise awareness and understanding of SCD, and work toward a brighter future for warriors and their communities. We are also proud to work with and support many organizations in the sickle cell community including:

Sickle Cell Disease Partnership
In addition, we are proud to be a founding member of the Sickle Cell Disease Partnership, which brings together members of the patient, provider and biopharmaceutical communities to advocate for policies that improve quality and access to care for the Sickle Cell Warriors.
Learn more about the partnership here.
Learn about our work in SCD
To learn more about our SCD studies in the U.S., visit our clinical trials website. For information about non-U.S. sites, visit clinicaltrials.gov.
We are with you: A message to the sickle cell community
Vertex is committed to the sickle cell disease community. Beyond our science, it’s about showing up and locking arms with the community to work together toward meaningful change.
Unraveling the hidden impacts of sickle cell disease and beta thalassemia
Understanding the real-life impacts of managing SCD and TDT.
A new Partnership to ignite change for sickle cell disease
The Sickle Cell Disease Partnership is a multistakeholder coalition, launched in June, which works to improve care and access for people living with sickle cell disease. Here, Chief Patient Officer Amit Sachdev discusses the partnership, its goals and the reasons it was founded.