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At Vertex Pharmaceuticals, we believe true scientific transformation happens at the intersection of human biology and medical innovation. One of the tools we leverage is CRISPR/Cas9, a technology that opens the door to gene editing. In this animation, you can learn more about how CRISPR/Cas9 works, and how it has the potential to be used in therapeutic development.

Our strategy at Vertex focuses on finding the tools and technologies we think we need to solve some of the most difficult medical and scientific problems. We're continuously developing and expanding this discovery toolbox, building upon our expertise, and ensuring we can use innovative scientific and drug development processes in the hopes of finding the best options for patients. With gene editing as one of our tools, we hope to impact genetic diseases where there is a high unmet need and limited treatment options available.

About this video series 

This series shares the science behind some of the tools and technologies we use in our research and clinical development. As our scientists continue to make progress, we want to spread awareness about the innovative technology used behind the scenes in our labs. Stay tuned to learn about some of the other tools in our toolbox that we are using to advance toward our goals.