Beta thalassemia

A father holding up his daughter sitting on his shoulders


Every day, people living with serious diseases strive to be more than their disease — to be defined by what they can dream and hope and achieve, not by what limits them. Our commitment to people with serious diseases is uncompromising and goes beyond our R&D and medicines. 

Working with the beta thalassemia community

We work with organizations that help people with transfusion-dependent beta thalassemia (TDT) live active, full lives.

We are committed to investigating and advancing approaches to treat the underlying cause of TDT. Vertex seeks to identify opportunities where we can support, empower, learn from and engage with the beta thalassemia community and ensure their voices are represented and incorporated into all that we do. 

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Supporting the beta thalassemia community

We are honored to support our beta thalassemia community partners to raise awareness and understanding of thalassemia, including Cooley’s Anemia Foundation, the Thalassemia International Federation and others. 

Our work in beta thalassemia 

Click here to learn more about our research in beta thalassemia.

To learn more about our beta thalassemia studies in the U.S., visit the clinical trials website.
For information about non-U.S. sites, visit