Vertex Forward: Illustrating Our Scientific Strategy
Follow along as we illustrate the science behind each disease in our pipeline, its underlying cause and how our work fits our strategy
At Vertex, we believe the most important medicines are those that have a transformative impact for patients. And while drug discovery and development are complicated processes, learning about our approach and the diseases in our pipeline doesn’t have to be. We’re excited to share this animated video series, “Vertex Forward: Illustrating our Scientific Strategy,” where you can see our philosophy and strategy explained. In the coming months, we’ll share additional videos to provide a glimpse into each disease within our pipeline, its underlying cause, and how we are working to invent potential treatments for each.
Illustrating Our Scientific Strategy
Learn about the Vertex research principles that are the connective thread behind everything we do — from discovering molecules to applying our work in the clinic — and our hopes for the future of our expanding pipeline.
Exploring APOL1-Mediated Kidney Diseases
See how inherited changes in the APOL1 gene can cause severe kidney diseases, including focal segmental glomerulosclerosis (FSGS), and how our scientists are working toward a potential treatment for APOL1-mediated FSGS.
Taking on AATD
Take a few minutes to learn about the inherited lung and liver disease alpha-1 antitrypsin deficiency (AATD), and see how we're using our expertise in protein folding (from our research in cystic fibrosis) as the foundation for our research for a potential treatment for AATD.
Our Focus on Hemoglobinopathies
Watch as we illustrate the underlying causes of both sickle cell disease and beta thalassemia and our work on an investigational gene-editing approach to potentially treat those living with these diseases.
Navigating Duchenne Muscular Dystrophy
Take a few minutes to learn about Duchenne muscular dystrophy (DMD) and see how we're investigating CRISPR gene-editing technology in the hopes of changing precise parts of the DMD gene.